Eugenio Montini

Milan, 20132, Italy

Last Updated: 09/26/2026

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Found 79 publications

Tweaking lentiviral vector design balances efficacy and safety in liver-directed gene therapy for familial hypercholesterolemia.

Tweaking lentiviral vector design balances efficacy and safety in liver-directed gene therapy for familial hypercholesterolemia.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: October 14, 2025

Ex vivo expansion of hematopoietic stem and progenitor cells from human mobilized peripheral blood for gene therapy applications.

Ex vivo expansion of hematopoietic stem and progenitor cells from human mobilized peripheral blood for gene therapy applications.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: October 10, 2025

Gene therapy supports long-term reconstitution of patient hematopoietic stem cells in deficiency of adenosine deaminase 2.

Gene therapy supports long-term reconstitution of patient hematopoietic stem cells in deficiency of adenosine deaminase 2.

Journal: Molecular therapy. Methods & clinical development

Published: September 16, 2025

In-depth characterization of stem cell potency and genotoxicity for clinical-scale ex vivo CRISPR-Cas9 gene editing.

In-depth characterization of stem cell potency and genotoxicity for clinical-scale ex vivo CRISPR-Cas9 gene editing.

Journal: Molecular therapy. Advances

Published: August 01, 2025

APOBEC3 and the mutational signature of lentiviral vectors.

APOBEC3 and the mutational signature of lentiviral vectors.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: June 29, 2025

RAAVioli: A comprehensive approach to characterizing AAV vector integrations and rearrangements.

RAAVioli: A comprehensive approach to characterizing AAV vector integrations and rearrangements.

Journal: Molecular therapy. Advances

Published: June 20, 2025

Tumor-targeted interferon-α gene therapy for glioblastoma: a phase 1 trial.

Tumor-targeted interferon-α gene therapy for glioblastoma: a phase 1 trial.

Journal: Nature medicine

Published: June 18, 2025

Nanoengineered 3D culture substrate enables superior persistence and polyclonal engraftment of genetically engineered hematopoietic stem cells.

Nanoengineered 3D culture substrate enables superior persistence and polyclonal engraftment of genetically engineered hematopoietic stem cells.

Journal: Cell stem cell

Published: June 18, 2025

Long-Term Effects of Atidarsagene Autotemcel for Metachromatic Leukodystrophy.

Long-Term Effects of Atidarsagene Autotemcel for Metachromatic Leukodystrophy.

Journal: The New England journal of medicine

Published: April 23, 2025

Liver-directed lentiviral gene therapy confers durable hepatic and systemic amelioration of methylmalonic acidemia in mice.

Liver-directed lentiviral gene therapy confers durable hepatic and systemic amelioration of methylmalonic acidemia in mice.

Journal: Journal of hepatology

Published: March 28, 2025

Response to: Safety and efficacy considerations of HSC-based gene therapy for RAG1-deficient SCID.

Response to: Safety and efficacy considerations of HSC-based gene therapy for RAG1-deficient SCID.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: March 12, 2025

Donor-derived CARCIK-CD19 cells engineered with Sleeping Beauty transposon in acute lymphoblastic leukemia relapsed after allogeneic transplantation.

Donor-derived CARCIK-CD19 cells engineered with Sleeping Beauty transposon in acute lymphoblastic leukemia relapsed after allogeneic transplantation.

Journal: Blood cancer journal

Published: January 08, 2025

Showing 1-12 of 79

Last Updated: 09/26/2026