Federica Rinaldi

University Walk
Bristol, ENG, United Kingdom

Last Updated: 09/26/2026

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Found 11 publications

Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates.

Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: October 08, 2022

A first-in-human phase I/IIa gene transfer clinical trial for Duchenne muscular dystrophy using rAAVrh74.MCK.GALGT2.

A first-in-human phase I/IIa gene transfer clinical trial for Duchenne muscular dystrophy using rAAVrh74.MCK.GALGT2.

Journal: Molecular therapy. Methods & clinical development

Published: October 18, 2021

RNA sequencing reveals MMP2 and TGFB1 downregulation in LRRK2 G2019S Parkinson's iPSC-derived astrocytes.

RNA sequencing reveals MMP2 and TGFB1 downregulation in LRRK2 G2019S Parkinson's iPSC-derived astrocytes.

Journal: Neurobiology of disease

Published: November 13, 2018

Gene Therapy Corrects Brain and Behavioral Pathologies in CLN6-Batten Disease.

Gene Therapy Corrects Brain and Behavioral Pathologies in CLN6-Batten Disease.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: November 13, 2018

Excess α-synuclein compromises phagocytosis in iPSC-derived macrophages.

Excess α-synuclein compromises phagocytosis in iPSC-derived macrophages.

Journal: Scientific reports

Published: April 12, 2017

High content analysis in amyotrophic lateral sclerosis.

High content analysis in amyotrophic lateral sclerosis.

Journal: Molecular and cellular neurosciences

Published: June 28, 2016

Enhanced efficacy of the CDNF/MANF family by combined intranigral overexpression in the 6-OHDA rat model of Parkinson's disease.

Enhanced efficacy of the CDNF/MANF family by combined intranigral overexpression in the 6-OHDA rat model of Parkinson's disease.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: July 01, 2014

Modeling astrocytic contribution toward neurodegeneration with pluripotent stem cells: focus on Alzheimer's and Parkinson's diseases.

Modeling astrocytic contribution toward neurodegeneration with pluripotent stem cells: focus on Alzheimer's and Parkinson's diseases.

Journal: Neuroreport

Published: November 09, 2013

Galanin promotes neuronal differentiation from neural progenitor cells in vitro and contributes to the generation of new olfactory neurons in the adult mouse brain.

Galanin promotes neuronal differentiation from neural progenitor cells in vitro and contributes to the generation of new olfactory neurons in the adult mouse brain.

Journal: Experimental neurology

Published: September 17, 2013

Cross-regulation of Connexin43 and β-catenin influences differentiation of human neural progenitor cells.

Cross-regulation of Connexin43 and β-catenin influences differentiation of human neural progenitor cells.

Journal: Cell death & disease

Published: May 20, 2013

Towards mature use of semantic resources for biomedical analyses.

Towards mature use of semantic resources for biomedical analyses.

Journal: Journal of biomedical semantics

Published: December 15, 2011

Showing 1-11 of 11

Last Updated: 09/26/2026