Francesca Tucci
Milan, Italy
Last Updated: 09/26/2026
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Found 31 publications
Ex vivo expansion of hematopoietic stem and progenitor cells from human mobilized peripheral blood for gene therapy applications.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: October 10, 2025
Development and characterization of a model of mucopolysaccharidosis type IVA for evaluating therapies targeting bone disease.
Journal: Disease models & mechanisms
Published: June 27, 2025
Long-Term Effects of Atidarsagene Autotemcel for Metachromatic Leukodystrophy.
Journal: The New England journal of medicine
Published: April 23, 2025
Hematopoietic stem cell gene therapy of neurometabolic lysosomal storage diseases.
Journal: Brain & development
Published: April 10, 2025
Non-neurological, non-skeletal outcomes after hematopoietic stem and progenitor cell-gene therapy (OTL-203) for Hurler syndrome.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: April 02, 2025
Ultrasonographic hip morphology in mucopolysaccharidosis type I Hurler after hematopoietic stem cell gene therapy.
Journal: Journal of children's orthopaedics
Published: September 11, 2024
Early skeletal outcomes after hematopoietic stem and progenitor cell gene therapy for Hurler syndrome.
Journal: Science translational medicine
Published: May 01, 2024
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID.
Journal: Nature communications
Published: October 13, 2023
Outcome of BCG Vaccination in ADA-SCID Patients: A 12-Patient Series.
Journal: Biomedicines
Published: May 15, 2023
Hemophagocytic inflammatory syndrome in ADA-SCID: report of two cases and literature review.
Journal: Frontiers in immunology
Published: March 16, 2023
Last Updated: 09/26/2026