Last Updated: 09/26/2026
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Found 5 publications
Amifampridine safety and efficacy in spinal muscular atrophy ambulatory patients: a randomized, placebo-controlled, crossover phase 2 trial.
Journal: Journal of neurology
Published: March 13, 2022
Therapeutic efficacy of 3,4-Diaminopyridine phosphate on neuromuscular junction in Pompe disease.
Journal: Biomedicine & pharmacotherapy = Biomedecine & pharmacotherapie
Published: December 04, 2020
Two-Dimensional Proton Magnetic Resonance Spectroscopy versus J-Editing for GABA Quantification in Human Brain: Insights from a GABA-Aminotransferase Inhibitor Study.
Journal: Scientific reports
Published: January 04, 2018
In Vivo Detection of CPP-115 Target Engagement in Human Brain.
Journal: Neuropsychopharmacology : official publication of the American College of Neuropsychopharmacology
Published: February 09, 2017
Acetylator Status Impacts Amifampridine Phosphate (Firdapse™) Pharmacokinetics and Exposure to a Greater Extent Than Renal Function.
Journal: Clinical therapeutics
Published: February 09, 2017
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Last Updated: 09/26/2026