Last Updated: 09/26/2026
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Found 5 publications
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1.
Journal: Obstetrical & gynecological survey
Published: December 30, 2025
Lentiviral Gene Therapy for Severe Leukocyte Adhesion Deficiency Type 1.
Journal: The New England journal of medicine
Published: April 30, 2025
Phase 1 Study of AAV9.LAMP2B Gene Therapy in Danon Disease.
Journal: The New England journal of medicine
Published: November 18, 2024
Systemic AAV9.LAMP2B injection reverses metabolic and physiologic multiorgan dysfunction in a murine model of Danon disease.
Journal: Science translational medicine
Published: February 28, 2019
Olaratumab and doxorubicin versus doxorubicin alone for treatment of soft-tissue sarcoma: an open-label phase 1b and randomised phase 2 trial.
Journal: Lancet (London, England)
Published: June 14, 2016
Showing 1-5 of 5
Last Updated: 09/26/2026