Last Updated: 09/26/2026
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Found 40 publications
Gene Therapy and Gene Editing for β-Thalassemia.
Journal: Hematology/oncology clinics of North America
Published: March 12, 2023
Clinical characteristics and outcomes of children with newly diagnosed acute myeloid leukemia and hyperleukocytosis managed with different cytoreductive methods.
Journal: Cancer
Published: September 09, 2022
Selumetinib for Refractory Pulmonary and Gastrointestinal Bleeding in Noonan Syndrome.
Journal: Pediatrics
Published: June 21, 2022
Effective therapies for sickle cell disease: are we there yet?
Journal: Trends in genetics : TIG
Published: April 11, 2022
Activation of γ-globin expression by hypoxia-inducible factor 1α.
Journal: Nature
Published: October 15, 2021
Personalized Clinical Research: Childhood Cancer Survivor and Parent Preferences for Research Participation.
Journal: JCO oncology practice
Published: October 02, 2020
Phase I Dose-Finding, Safety, and Tolerability Trial of Romiplostim to Improve Platelet Recovery After UCB Transplantation.
Journal: Transplantation and cellular therapy
Published: September 01, 2020
Last Updated: 09/26/2026