Giada De Ponti
Milan, 20132, Italy
Last Updated: 09/26/2026
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Found 8 publications
Development and characterization of a model of mucopolysaccharidosis type IVA for evaluating therapies targeting bone disease.
Journal: Disease models & mechanisms
Published: June 27, 2025
Neonatal gene therapy effectively prevents disease manifestations in a murine model of Mucopolysaccharidosis type I.
Journal: Molecular therapy. Methods & clinical development
Published: June 11, 2024
Transcriptomic analysis of BM-MSCs identified EGR1 as a transcription factor to fully exploit their therapeutic potential.
Journal: Biochimica et biophysica acta. Molecular cell research
Published: April 24, 2024
A GLB1 transgene with enhanced therapeutic potential for the preclinical development of ex-vivo gene therapy to treat mucopolysaccharidosis type IVB.
Journal: Molecular therapy. Methods & clinical development
Published: February 13, 2024
MPSI Manifestations and Treatment Outcome: Skeletal Focus.
Journal: International journal of molecular sciences
Published: July 27, 2022
Role of ex vivo Expanded Mesenchymal Stromal Cells in Determining Hematopoietic Stem Cell Transplantation Outcome.
Journal: Frontiers in cell and developmental biology
Published: February 09, 2021
Neonatal combination therapy improves some of the clinical manifestations in the Mucopolysaccharidosis type I murine model.
Journal: Molecular genetics and metabolism
Published: January 31, 2020
Acute myeloid leukaemia niche regulates response to L-asparaginase.
Journal: British journal of haematology
Published: December 02, 2018
Showing 1-8 of 8
Last Updated: 09/26/2026