Giorgia Santilli
London, ENG, United Kingdom
Last Updated: 09/26/2026
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Found 42 publications
In vivo delivery strategies for therapeutic CRISPR genome editing.
Journal: International journal of biological sciences
Published: February 14, 2026
A modified cyclosporine enhances lentivector transduction ex vivo and in vivo by degrading IFITM3.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: January 21, 2026
In-depth characterization of stem cell potency and genotoxicity for clinical-scale ex vivo CRISPR-Cas9 gene editing.
Journal: Molecular therapy. Advances
Published: August 01, 2025
The future of ex vivo hematopoietic stem cell gene editing: what's next.
Journal: Regenerative medicine
Published: March 26, 2025
Unveiling the cut-and-repair cycle of designer nucleases in human stem and T cells via CLEAR-time dPCR.
Journal: Nature communications
Published: December 17, 2024
Therapeutic activity of a hematopoietic stem cell-delivered cell-penetrating frataxin in Friedreich's ataxia models.
Journal: Cell reports. Medicine
Published: November 11, 2024
Tailoring capsid-directed evolution technology for improved AAV-mediated CAR-T generation.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: March 25, 2024
Multidimensional Response Surface Methodology for the Development of a Gene Editing Protocol for p67phox-Deficient Chronic Granulomatous Disease.
Journal: Human gene therapy
Published: December 08, 2023
Hematopoietic stem cell gene editing rescues B-cell development in X-linked agammaglobulinemia.
Journal: The Journal of allergy and clinical immunology
Published: December 01, 2023
Myelodysplasia and transgene inactivation in X-CGD-γ retroviral gene therapy: The usual suspects and new players.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: November 06, 2023
AAV capsid bioengineering in primary human retina models.
Journal: Scientific reports
Published: August 24, 2023
Assessment of Pre-Clinical Liver Models Based on Their Ability to Predict the Liver-Tropism of Adeno-Associated Virus Vectors.
Journal: Human gene therapy
Published: March 17, 2023
Last Updated: 09/26/2026