Last Updated: 09/26/2026
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Found 7 publications
Deficiency of galactosyl-ceramidase in adult oligodendrocytes worsens disease severity during chronic experimental allergic encephalomyelitis.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: December 14, 2023
Preclinical studies in Krabbe disease: A model for the investigation of novel combination therapies for lysosomal storage diseases.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: March 26, 2022
Waning efficacy in a long-term AAV-mediated gene therapy study in the murine model of Krabbe disease.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: November 04, 2020
AAV-Mediated GALC Gene Therapy Rescues Alpha-Synucleinopathy in the Spinal Cord of a Leukodystrophic Lysosomal Storage Disease Mouse Model.
Journal: Frontiers in cellular neuroscience
Published: October 20, 2020
Oncolytic adenovirus Ad657 for systemic virotherapy against prostate cancer.
Journal: Oncolytic virotherapy
Published: May 17, 2018
SAFETY AND TOLERABILITY OF MRI-GUIDED INFUSION OF AAV2-hAADC INTO THE MID-BRAIN OF NON-HUMAN PRIMATE.
Journal: Molecular therapy. Methods & clinical development
Published: December 27, 2014
AAV9-mediated expression of a non-self protein in nonhuman primate central nervous system triggers widespread neuroinflammation driven by antigen-presenting cell transduction.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: May 14, 2013
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Last Updated: 09/26/2026