Last Updated: 09/26/2026
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Found 45 publications
Real-World Data on the Effectiveness and Safety of wilate for the Treatment of von Willebrand Disease.
Journal: TH open : companion journal to thrombosis and haemostasis
Published: October 30, 2020
Comorbidities and complications in adults with pyruvate kinase deficiency.
Journal: European journal of haematology
Published: October 05, 2020
Characterization of the severe phenotype of pyruvate kinase deficiency.
Journal: American journal of hematology
Published: June 27, 2020
Genotype-phenotype correlation and molecular heterogeneity in pyruvate kinase deficiency.
Journal: American journal of hematology
Published: January 13, 2020
Safety and Efficacy of Mitapivat in Pyruvate Kinase Deficiency.
Journal: The New England journal of medicine
Published: September 05, 2019
Ferritin in serum and urine: A pilot study.
Journal: Blood cells, molecules & diseases
Published: December 27, 2018
Safety and efficacy of turoctocog alfa in the prevention and treatment of bleeds in previously untreated paediatric patients with severe haemophilia A: Results from the guardian 4 multinational clinical trial.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: December 20, 2018
Prevalence and management of iron overload in pyruvate kinase deficiency: report from the Pyruvate Kinase Deficiency Natural History Study.
Journal: Haematologica
Published: September 15, 2018
Acute neonatal bilirubin encephalopathy in the State of Utah 2009-2018.
Journal: Blood cells, molecules & diseases
Published: May 11, 2018
Fetal presentation of congenital dyserythropoietic anemia type 1 with novel compound heterozygous CDAN1 mutations.
Journal: Blood cells, molecules & diseases
Published: March 16, 2018
Last Updated: 09/26/2026