Hernan D. Gonorazky

Toronto, ON, Canada

Last Updated: 09/26/2026

Save publications for later

Sign Up

Not sure about your diagnosis?

Check Your Symptoms

Found 62 publications

Expanding Vamorolone Treatment Access for Canadians with Duchenne Muscular Dystrophy.

Expanding Vamorolone Treatment Access for Canadians with Duchenne Muscular Dystrophy.

Journal: The Canadian journal of neurological sciences. Le journal canadien des sciences neurologiques

Published: July 13, 2026

Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys.

Vamorolone Safety, Pharmacokinetics, and Exploratory Efficacy in Duchenne Muscular Dystrophy: A Phase II, Nonrandomized, Multiple-Dose Study in 2-<4-Year-Old Boys.

Journal: Neurology

Published: May 15, 2026

Factors Impacting Outcomes of Peripheral Nerve Blockade in Children With Charcot-Marie-Tooth Disease Undergoing Foot Surgery.

Factors Impacting Outcomes of Peripheral Nerve Blockade in Children With Charcot-Marie-Tooth Disease Undergoing Foot Surgery.

Journal: Paediatric anaesthesia

Published: December 11, 2025

Severe neonatal-onset PYROXD1-related myopathy with a novel homozygous missense variant: expanding the phenotypic spectrum.

Severe neonatal-onset PYROXD1-related myopathy with a novel homozygous missense variant: expanding the phenotypic spectrum.

Journal: Neuromuscular disorders : NMD

Published: December 03, 2025

Results of a phase II open-label, multiple-dose study of vamorolone (VBP15-006) in 7- to < 18-year-old boys with duchenne muscular dystrophy.

Results of a phase II open-label, multiple-dose study of vamorolone (VBP15-006) in 7- to < 18-year-old boys with duchenne muscular dystrophy.

Journal: Journal of neurology

Published: November 11, 2025

Salbutamol in Congenital Myasthenic Syndrome: A Systematic Review.

Salbutamol in Congenital Myasthenic Syndrome: A Systematic Review.

Journal: BMC neurology

Published: September 16, 2025

Understanding the experiences of adults with spinal muscular atrophy & their transition to an adult program: A mixed methods study.

Understanding the experiences of adults with spinal muscular atrophy & their transition to an adult program: A mixed methods study.

Journal: Journal of neuromuscular diseases

Published: September 15, 2025

Disease-modifying therapies for spinal muscular atrophy: Family experience, ethical considerations, and the role of social determinants of health.

Disease-modifying therapies for spinal muscular atrophy: Family experience, ethical considerations, and the role of social determinants of health.

Journal: Journal of neuromuscular diseases

Published: September 03, 2025

Clinical validity of congenital myopathy genes determined by the ClinGen Congenital Myopathies Expert Panel.

Clinical validity of congenital myopathy genes determined by the ClinGen Congenital Myopathies Expert Panel.

Journal: Journal of neuromuscular diseases

Published: June 10, 2025

Pediatric Cohort of Charcot-Marie-Tooth Disease: Clinical Features and Genetic Distribution.

Pediatric Cohort of Charcot-Marie-Tooth Disease: Clinical Features and Genetic Distribution.

Journal: Neurology. Genetics

Published: May 16, 2025

Respiratory and Bulbar Support in Spinal Muscular Atrophy Type I Treated with Nusinersen.

Respiratory and Bulbar Support in Spinal Muscular Atrophy Type I Treated with Nusinersen.

Journal: The Canadian journal of neurological sciences. Le journal canadien des sciences neurologiques

Published: May 13, 2025

Weakness, Abdominal and Limb Pain in a 17-Year-Old With Type 1 Diabetes.

Weakness, Abdominal and Limb Pain in a 17-Year-Old With Type 1 Diabetes.

Journal: Journal of paediatrics and child health

Published: April 10, 2025

Showing 1-12 of 62

Last Updated: 09/26/2026