Last Updated: 09/26/2026
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Found 30 publications
Navigating sexual health, fertility, and adult wellness in individuals with Duchenne muscular dystrophy: Current standards of care and future directions.
Journal: Journal of neuromuscular diseases
Published: July 13, 2026
Identification of novel protein biomarkers correlating with both cardiac and skeletal muscle indices in duchenne muscular dystrophy.
Journal: Journal of neuromuscular diseases
Published: April 15, 2026
Assessing movement quality in individuals with Duchenne muscular dystrophy utilizing accelerometry: Comparisons with healthy controls.
Journal: PLOS digital health
Published: March 05, 2026
Safety and efficacy of individualised exercise and NAD+ precursor supplementation in patients with Friedreich's ataxia in the USA: a single-centre, 2 × 2 factorial, randomised controlled trial.
Journal: The Lancet. Neurology
Published: January 12, 2026
Proteomic signatures of pediatric cardiovascular and cardiometabolic traits demonstrate long-term modifiable drivers of adult disease.
Journal: medRxiv : the preprint server for health sciences
Published: November 24, 2025
Optimizing Care for Growth and Puberty in Duchenne Muscular Dystrophy: A Survey of Clinical Practice in the OPTIMIZE DMD Consortium.
Journal: Muscle & nerve
Published: September 04, 2025
Adrenal Suppression in Duchenne Muscular Dystrophy: Management Strategies Incorporating Novel Steroid Vamorolone.
Journal: Journal of the Endocrine Society
Published: June 18, 2025
Natural History of Hyperphagia in Patients with Pseudohypoparathyroidism.
Journal: Journal of clinical medicine
Published: June 11, 2025
Examining androgen and estrogen profiles during pubertal development in autistic and neurotypical girls.
Journal: Hormones and behavior
Published: March 11, 2025
Physical activity and cardiac function in patients with Duchenne muscular dystrophy.
Journal: Cardiology in the young
Published: February 27, 2025
Cardiovascular-Kidney-Metabolic Disease Burden in Children and Adults Following Heart Transplantation.
Journal: JACC. Heart failure
Published: February 25, 2025
Last Updated: 09/26/2026