Jacob G. Mikkelsen
Arhus, Denmark
Last Updated: 09/26/2026
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Found 89 publications
AAV vector production in suspension cells using PEI transfection and sodium butyrate with orthogonal assessment of function and quality.
Journal: Molecular therapy. Advances
Published: December 16, 2025
CRISPR/Cas gene editing of haematopoietic stem cells for curing primary immunodeficiency
Journal: Ugeskrift for laeger
Published: June 20, 2025
CXCR2 deficiency with myelokathexis caused by a novel variant: correction via CRISPR/Cas9.
Journal: Haematologica
Published: May 07, 2025
Trojan Horse-Like Vehicles for CRISPR-Cas Delivery: Engineering Extracellular Vesicles and Virus-Like Particles for Precision Gene Editing in Cystic Fibrosis.
Journal: Human gene therapy
Published: April 28, 2025
PKP1 promotes lung cancer by modulating energy metabolism through stabilization of PFKP.
Journal: Biomarker research
Published: March 07, 2025
Genetically heterozygous - transcriptionally homozygous IRF7 deficiency underlies herpesvirus CNS infections in humans.
Journal: The Journal of experimental medicine
Published: March 04, 2025
Multiparametric Optimization of Human Primary B-Cell Cultures Using Design of Experiments.
Journal: Scandinavian journal of immunology
Published: January 20, 2025
Treatment of GATA2 deficiency by allele-specific CRISPR-Cas9-directed gene correction in hematopoietic stem cells.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: December 20, 2024
Gene editing in hematopoietic stem cells by co-delivery of Cas9/sgRNA ribonucleoprotein and templates for homology-directed repair in 'all-in-one' lentivirus-derived nanoparticles.
Journal: Nucleic acids research
Published: November 25, 2024
Gene Editing by Ferrying of CRISPR/Cas Ribonucleoprotein Complexes in Enveloped Virus-Derived Particles.
Journal: Human gene therapy
Published: August 16, 2024
Last Updated: 09/26/2026