Last Updated: 09/26/2026
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Found 27 publications
Carbetocin Nasal Spray for the Treatment of Hyperphagia in Prader-Willi Syndrome: Results From the Randomized, Placebo-Controlled, Phase 3 Compass PWS Study.
Journal: Clinical therapeutics
Published: April 23, 2026
A Phase 1, Randomized, Open-Label Study to Assess the Bioequivalence of Trofinetide as a Ready-to-Use Oral Solution and Constituted Powder for Oral Solution in Healthy Adults.
Journal: Advances in therapy
Published: October 01, 2025
Physiologically-Based Pharmacokinetic Modeling of Trofinetide in Moderate Renal Impairment for Phase 1 Clinical Study Dose Selection with Model Validation.
Journal: European journal of drug metabolism and pharmacokinetics
Published: October 16, 2024
International workshop: what is needed to ensure outcome measures for Rett syndrome are fit-for-purpose for clinical trials? June 7, 2023, Nashville, USA.
Journal: Trials
Published: September 12, 2024
Population Pharmacokinetics of Trofinetide in a Pediatric Population Aged 2-4 Years with Rett Syndrome.
Journal: Advances in therapy
Published: September 06, 2024
Population Pharmacokinetic Modeling to Support Trofinetide Dosing for the Treatment of Rett Syndrome.
Journal: Advances in therapy
Published: August 22, 2024
Results from the phase 2/3 DAFFODIL study of trofinetide in girls aged 2-4 years with Rett syndrome.
Results from the phase 2/3 DAFFODIL study of trofinetide in girls aged 2-4 years with Rett syndrome.
Journal: Med (New York, N.Y.)
Published: July 25, 2024
Trofinetide for the treatment of Rett syndrome: Long-term safety and efficacy results of the 32-month, open-label LILAC-2 study.
Journal: Med (New York, N.Y.)
Published: March 15, 2024
Development of trofinetide for the treatment of Rett syndrome: from bench to bedside.
Journal: Frontiers in pharmacology
Published: November 20, 2023
Gastrointestinal manifestations in pediatric and adult patients with Rett syndrome: an analysis of US claims and physician survey data.
Journal: Journal of comparative effectiveness research
Published: November 16, 2023
Last Updated: 09/26/2026