Last Updated: 09/26/2026
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Found 28 publications
Gene therapy approaches for inborn errors of immunity: from bench to bedside.
Journal: Expert opinion on biological therapy
Published: July 25, 2026
Improved outcome of HSCT in STAT1 gain-of-function disease following JAK inhibition bridging.
Journal: Journal of human immunity
Published: October 27, 2025
Newborn screening reduces survival disparities in SCID after stem cell transplant: A PIDTC report.
Journal: Journal of human immunity
Published: October 27, 2025
Cyclophosphamide and Thiotepa Increases Risk of Transplant-Associated Thrombotic Microangiopathy.
Journal: Transplantation and cellular therapy
Published: March 20, 2024
Relevance of lymphocyte proliferation to PHA in severe combined immunodeficiency (SCID) and T cell lymphopenia.
Journal: Clinical immunology (Orlando, Fla.)
Published: December 28, 2023
Diagnosing and Grading of Sinusoidal Obstructive Syndrome after Hematopoietic Stem Cell Transplant of Children, Adolescent and Young Adults treated in a Pediatric Institution with Pediatric Protocols.
Journal: Transplantation and cellular therapy
Published: October 06, 2023
JAK inhibitor treatment for inborn errors of JAK/STAT signaling: An ESID/EBMT-IEWP retrospective study.
Journal: The Journal of allergy and clinical immunology
Published: July 21, 2023
Posttransplantation late complications increase over time for patients with SCID: A Primary Immune Deficiency Treatment Consortium (PIDTC) landmark study.
Journal: The Journal of allergy and clinical immunology
Published: March 30, 2023
Lentiviral Gene Therapy for Artemis-Deficient SCID.
Journal: The New England journal of medicine
Published: December 22, 2022
Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium.
Journal: Lancet (London, England)
Published: December 09, 2022
Last Updated: 09/26/2026