Jennifer A. Braun

Pediatrics | Pediatric Hematology Oncology
2450 Riverside Avenue
Building 9 EAST
Minneapolis, MN 55454

Last Updated: 09/26/2026

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Found 2 publications

Biomarker changes in cerebral adrenoleukodystrophy after gene therapy or allogeneic hematopoietic cell transplant.

Biomarker changes in cerebral adrenoleukodystrophy after gene therapy or allogeneic hematopoietic cell transplant.

Journal: Molecular therapy. Advances
Published: May 21, 2026

Secondary failure of lentiviral vector gene therapy in a cerebral adrenoleukodystrophy patient with an ABCD1 whole-gene deletion.

Secondary failure of lentiviral vector gene therapy in a cerebral adrenoleukodystrophy patient with an ABCD1 whole-gene deletion.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: June 14, 2024
Showing 1-2 of 2

Last Updated: 09/26/2026