Last Updated: 09/26/2026
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Found 57 publications
Mitapivat in adults with non-transfusion-dependent α-thalassaemia or β-thalassaemia (ENERGIZE): a phase 3, international, randomised, double-blind, placebo-controlled trial.
Journal: Lancet (London, England)
Published: November 08, 2024
Long-term efficacy and safety of mitapivat in non-transfusion-dependent α- or β-thalassaemia: An open-label phase 2 study.
Journal: British journal of haematology
Published: October 10, 2024
Changes in indicators of cerebral metabolic stress following treatment with voxelotor in children and adolescents with sickle cell anemia.
Journal: EJHaem
Published: May 15, 2024
A Novel One-Sample Mendelian Randomization Approach for Count-Type Outcomes That Is Robust to Correlated and Uncorrelated Pleiotropic Effects.
Journal: Genetic epidemiology
Published: March 09, 2024
Genetic Variation and Sickle Cell Disease Severity: A Systematic Review and Meta-Analysis.
Journal: JAMA network open
Published: October 18, 2023
Intensive hydroxyurea dosing in very young children with sickle cell anemia.
Journal: Blood advances
Published: January 05, 2023
Barriers and Facilitators of Premarital Genetic Counseling for Sickle Cell Disease in Northern Nigeria.
Journal: Journal of pediatric hematology/oncology
Published: October 18, 2022
Working memory and school readiness in preschool children with sickle cell disease compared to demographically matched controls.
Journal: British journal of haematology
Published: July 01, 2022
Strategies to increase access to basic sickle cell disease care in low- and middle-income countries.
Strategies to increase access to basic sickle cell disease care in low- and middle-income countries.
Journal: Expert review of hematology
Published: April 11, 2022
Last Updated: 09/26/2026