Johan Deniaud
UMR 703, Oniris, INRAE, Route De Gachet, CS 40706
Nantes, 44307, France
Nantes, 44307, France
Last Updated: 09/26/2026
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Found 8 publications
Accumulation of membrane repair-associated proteins and mature myostatin are novel markers of muscle pathophysiology in Pompe disease.
Journal: Acta neuropathologica communications
Published: January 14, 2026
Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases?
Journal: Molecular therapy. Methods & clinical development
Published: March 10, 2020
Satellite cells fail to contribute to muscle repair but are functional in Pompe disease (glycogenosis type II).
Journal: Acta neuropathologica communications
Published: August 17, 2018
Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease.
Journal: Acta neuropathologica communications
Published: July 21, 2017
Efficient CNS targeting in adult mice by intrathecal infusion of single-stranded AAV9-GFP for gene therapy of neurological disorders.
Journal: Gene therapy
Published: November 11, 2016
Intracerebral Gene Therapy Using AAVrh.10-hARSA Recombinant Vector to Treat Patients with Early-Onset Forms of Metachromatic Leukodystrophy: Preclinical Feasibility and Safety Assessments in Nonhuman Primates.
Journal: Human gene therapy. Clinical development
Published: March 12, 2015
Intracisternal delivery of AAV9 results in oligodendrocyte and motor neuron transduction in the whole central nervous system of cats.
Journal: Gene therapy
Published: August 13, 2013
Showing 1-8 of 8
Last Updated: 09/26/2026