Last Updated: 09/26/2026
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Found 4 publications
A plain language summary of the SAPPHIRE clinical trial of apitegromab in children and young adults with spinal muscular atrophy.
Journal: Expert review of neurotherapeutics
Published: November 13, 2025
Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trial.
Journal: The Lancet. Neurology
Published: March 25, 2025
Advances and limitations for the treatment of spinal muscular atrophy.
Journal: BMC pediatrics
Published: December 12, 2021
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Last Updated: 09/26/2026