Kamal E. Gadalla
Edinburgh, SCT EH89XD, United Kingdom
Last Updated: 09/26/2026
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Found 11 publications
FMR1 gene therapy restores activity-driven inhibition and prevents audiogenic seizures in Fmr1 -/y mice.
Journal: bioRxiv : the preprint server for biology
Published: June 29, 2026
AAV9-Mediated PTEN Gene Therapy Rescues Hepatic Pathology and Neuroanatomical Abnormalities in a Murine Model of PTEN Hamartoma Tumour Syndrome.
Journal: Pharmaceutics
Published: June 03, 2026
Self-regulating gene therapy ameliorates phenotypes and overcomes gene dosage sensitivity in a mouse model of Rett syndrome.
Journal: Science translational medicine
Published: April 02, 2025
Inhibition of Piezo1 attenuates demyelination in the central nervous system.
Journal: Glia
Published: February 21, 2019
Reduced axonal diameter of peripheral nerve fibers in a mouse model of Rett syndrome.
Journal: Neuroscience
Published: March 31, 2017
Radically truncated MeCP2 rescues Rett syndrome-like neurological defects.
Journal: Nature
Published: March 29, 2017
Improved MECP2 Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal Delivery.
Journal: Molecular therapy. Methods & clinical development
Published: February 24, 2017
Development of a Novel AAV Gene Therapy Cassette with Improved Safety Features and Efficacy in a Mouse Model of Rett Syndrome.
Journal: Molecular therapy. Methods & clinical development
Published: February 24, 2017
Improved survival and reduced phenotypic severity following AAV9/MECP2 gene transfer to neonatal and juvenile male Mecp2 knockout mice.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: September 27, 2012
Showing 1-11 of 11
Last Updated: 09/26/2026