Last Updated: 09/26/2026
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Found 7 publications
Deramiocel heart-derived cellular therapy in advanced Duchenne muscular dystrophy (HOPE-3): a phase 3, randomised, double-blind, placebo-controlled trial.
Journal: Lancet (London, England)
Published: March 26, 2026
Transitions From Pediatric to Adult Neuromuscular Care: A Practical Guide.
Journal: Muscle & nerve
Published: June 24, 2025
The Pitfalls of Cardiac Troponin T Testing in Muscular Dystrophy.
Journal: The journal of applied laboratory medicine
Published: January 23, 2024
Continued safety and long-term effectiveness of onasemnogene abeparvovec in Ohio.
Journal: Neuromuscular disorders : NMD
Published: August 28, 2023
Assessment of the relationship between disease progression and goals of care by individuals with Duchenne muscular dystrophy and their caregivers.
Journal: Muscle & nerve
Published: June 16, 2021
Gene Therapy for Spinal Muscular Atrophy: Safety and Early Outcomes.
Journal: Pediatrics
Published: June 19, 2020
Showing 1-7 of 7
Last Updated: 09/26/2026