Last Updated: 09/26/2026
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Found 36 publications
Exposure-response of serum biomarkers to vamorolone, a dissociative corticosteroidal anti-inflammatory drug, in 4- to <7-year children.
Journal: Steroids
Published: August 11, 2025
Outcomes in Adult Inflammatory Bowel Disease Clinical Trials: Assessment of Similarity Among Participants with Adolescent-onset and Adult-onset Disease.
Journal: Journal of Crohn's & colitis
Published: November 12, 2023
Using multiple imputation of real-world data to estimate clinical remission in pediatric inflammatory bowel disease.
Journal: Journal of comparative effectiveness research
Published: February 17, 2023
Towards the international interoperability of clinical research networks for rare diseases: recommendations from the IRDiRC Task Force.
Journal: Orphanet journal of rare diseases
Published: August 01, 2022
Innovations in Pediatric Therapeutics Development: Principles for the Use of Bridging Biomarkers in Pediatric Extrapolation.
Journal: Therapeutic innovation & regulatory science
Published: June 01, 2022
Validating the Simplified Endoscopic Mucosal Assessment for Crohn's Disease: A Novel Method for Assessing Disease Activity.
Journal: Inflammatory bowel diseases
Published: April 11, 2022
The Role of Master Protocols in Pediatric Drug Development.
Journal: Therapeutic innovation & regulatory science
Published: March 18, 2022
Early Inflammatory Markers are Associated With Inadequate Post-Induction Infliximab Trough in Pediatric Crohn's Disease.
Journal: Journal of pediatric gastroenterology and nutrition
Published: January 13, 2021
Serum miRNAs Are Pharmacodynamic Biomarkers Associated With Therapeutic Response in Pediatric Inflammatory Bowel Disease.
Journal: Inflammatory bowel diseases
Published: April 23, 2020
Serum biomarkers associated with baseline clinical severity in young steroid-naïve Duchenne muscular dystrophy boys.
Journal: Human molecular genetics
Published: March 30, 2020
Last Updated: 09/26/2026