Last Updated: 09/26/2026
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Found 12 publications
An Antibody-Oligonucleotide Conjugate for Myotonic Dystrophy Type 1.
Journal: The New England journal of medicine
Published: February 18, 2026
Delpacibart Etedesiran Improves the Molecular Pathology of Myotonic Dystrophy Type 1 in the Phase 1/2 MARINA® Study.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: November 07, 2025
Delpacibart etedesiran improves the molecular pathology of myotonic dystrophy type 1 in the phase 1/2 MARINA study.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: November 07, 2025
Design and Rationale of the Global Phase 3 NEURO-TTRansform Study of Antisense Oligonucleotide AKCEA-TTR-LRx (ION-682884-CS3) in Hereditary Transthyretin-Mediated Amyloid Polyneuropathy.
Journal: Neurology and therapy
Published: December 02, 2020
Underlying Immune Disorder May Predispose Some Transthyretin Amyloidosis Subjects to Inotersen-Mediated Thrombocytopenia.
Journal: Nucleic acid therapeutics
Published: February 12, 2020
Cardiovascular and Metabolic Effects of ANGPTL3 Antisense Oligonucleotides.
Journal: The New England journal of medicine
Published: May 25, 2017
Addressing Unmet Medical Needs in Type 1 Diabetes: A Review of Drugs Under Development.
Journal: Current diabetes reviews
Published: December 22, 2015
Addressing unmet medical needs in type 2 diabetes: a narrative review of drugs under development.
Journal: Current diabetes reviews
Published: November 17, 2014
Higher mortality in patients with right hemispheric intracerebral haemorrhage: INTERACT1 and 2.
Journal: Journal of neurology, neurosurgery, and psychiatry
Published: November 06, 2014
Mechanisms of vascular dysfunction in mice with endothelium-specific deletion of the PPAR-δ gene.
Journal: American journal of physiology. Heart and circulatory physiology
Published: February 04, 2014
Showing 1-12 of 12
Last Updated: 09/26/2026