Last Updated: 09/26/2026
Save publications for later
Sign Up
Not sure about your diagnosis?
Check Your Symptoms
Found 14 publications
Nexiguran Ziclumeran Gene Editing in Hereditary ATTR with Polyneuropathy.
Journal: The New England journal of medicine
Published: September 26, 2025
CRISPR-Cas9 Gene Editing with Nexiguran Ziclumeran for ATTR Cardiomyopathy.
Journal: The New England journal of medicine
Published: November 18, 2024
Proteinuria as an End Point in Clinical Trials of Focal Segmental Glomerulosclerosis.
Journal: American journal of kidney diseases : the official journal of the National Kidney Foundation
Published: May 29, 2024
Developing an Edema Clinician-Reported Outcome Measure for Nephrotic Syndrome.
Journal: Glomerular diseases
Published: January 11, 2022
Health-Related Quality of Life in Focal Segmental Glomerular Sclerosis and Minimal Change Disease: A Qualitative Study of Children and Adults to Inform Patient-Reported Outcomes.
Journal: Kidney medicine
Published: August 17, 2021
Safety and Efficacy of GFB-887, a TRPC5 Channel Inhibitor, in Patients With Focal Segmental Glomerulosclerosis, Treatment-Resistant Minimal Change Disease, or Diabetic Nephropathy: TRACTION-2 Trial Design.
Journal: Kidney international reports
Published: April 12, 2021
Proteinuria Reduction and Kidney Survival in Focal Segmental Glomerulosclerosis.
Journal: American journal of kidney diseases : the official journal of the National Kidney Foundation
Published: September 06, 2019
AAV5-Factor VIII Gene Transfer in Severe Hemophilia A.
Journal: The New England journal of medicine
Published: December 12, 2017
Estimating the Effect of Preventable Treatment Discontinuation on Health Outcomes.
Journal: Epidemiology (Cambridge, Mass.)
Published: October 10, 2017
A study on the safety and efficacy of reveglucosidase alfa in patients with late-onset Pompe disease.
Journal: Orphanet journal of rare diseases
Published: December 07, 2016
Current unmet needs in renal transplantation: a review of challenges and therapeutics.
Journal: Frontiers in bioscience (Elite edition)
Published: December 29, 2015
Last Updated: 09/26/2026