Last Updated: 09/26/2026
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Found 4 publications
Spliceosome-Mediated Pre-mRNA trans-Splicing Can Repair CEP290 mRNA.
Journal: Molecular therapy. Nucleic acids
Published: December 14, 2017
RNA Trans-Splicing Targeting Endogenous β-Globin Pre-Messenger RNA in Human Erythroid Cells.
Journal: Human gene therapy methods
Published: March 08, 2017
Development of Polypeptide-based Nanoparticles for Non-viral Delivery of CD22 RNA Trans-splicing Molecule as a New Precision Medicine Candidate Against B-lineage ALL.
Journal: EBioMedicine
Published: March 27, 2015
CD22ΔE12 as a molecular target for corrective repair using RNA trans-splicing: anti-leukemic activity of a rationally designed RNA trans-splicing molecule.
Journal: Integrative biology : quantitative biosciences from nano to macro
Published: January 09, 2015
Showing 1-4 of 4
Last Updated: 09/26/2026