Last Updated: 09/26/2026
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Found 21 publications
A first-in-human phase I/IIa gene transfer clinical trial for Duchenne muscular dystrophy using rAAVrh74.MCK.GALGT2.
Journal: Molecular therapy. Methods & clinical development
Published: October 18, 2021
Gene Delivery for Limb-Girdle Muscular Dystrophy Type 2D by Isolated Limb Infusion.
Journal: Human gene therapy
Published: March 07, 2019
Bridging from Intramuscular to Limb Perfusion Delivery of rAAV: Optimization in a Non-human Primate Study.
Journal: Molecular therapy. Methods & clinical development
Published: November 13, 2018
Predicting Risk of Infection in Infants with Congenital Diaphragmatic Hernia.
Journal: The Journal of pediatrics
Published: May 29, 2018
An Isolated Limb Infusion Method Allows for Broad Distribution of rAAVrh74.MCK.GALGT2 to Leg Skeletal Muscles in the Rhesus Macaque.
Journal: Molecular therapy. Methods & clinical development
Published: January 04, 2018
Acquired Infection and Antimicrobial Utilization During Initial NICU Hospitalization in Infants With Congenital Diaphragmatic Hernia.
Journal: The Pediatric infectious disease journal
Published: December 01, 2017
Safety and Efficacy of AAV Retrograde Pancreatic Ductal Gene Delivery in Normal and Pancreatic Cancer Mice.
Journal: Molecular therapy. Methods & clinical development
Published: June 08, 2017
Induction of T-Cell Infiltration and Programmed Death Ligand 2 Expression by Adeno-Associated Virus in Rhesus Macaque Skeletal Muscle and Modulation by Prednisone.
Journal: Human gene therapy
Published: March 28, 2017
Short-term weight gain velocity in infants with congenital diaphragmatic hernia (CDH).
Journal: Early human development
Published: October 04, 2016
An arginase-1 SNP that protects against the development of pulmonary hypertension in bronchopulmonary dysplasia enhances NO-mediated apoptosis in lymphocytes.
Journal: Physiological reports
Published: August 18, 2016
Hypoxic proliferation requires EGFR-mediated ERK activation in human pulmonary microvascular endothelial cells.
Journal: American journal of physiology. Lung cellular and molecular physiology
Published: June 27, 2016
Predicting death or extended length of stay in infants with congenital diaphragmatic hernia.
Journal: Journal of perinatology : official journal of the California Perinatal Association
Published: October 07, 2015
Last Updated: 09/26/2026