Maddalena Migliavacca
Milan, Italy
Last Updated: 09/26/2026
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Found 31 publications
Long-Term Effects of Atidarsagene Autotemcel for Metachromatic Leukodystrophy.
Journal: The New England journal of medicine
Published: April 23, 2025
Early skeletal outcomes after hematopoietic stem and progenitor cell gene therapy for Hurler syndrome.
Journal: Science translational medicine
Published: May 01, 2024
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID.
Journal: Nature communications
Published: October 13, 2023
Outcome of BCG Vaccination in ADA-SCID Patients: A 12-Patient Series.
Journal: Biomedicines
Published: May 15, 2023
Hemophagocytic inflammatory syndrome in ADA-SCID: report of two cases and literature review.
Journal: Frontiers in immunology
Published: March 16, 2023
Case Report: Consistent disease manifestations with a staggered time course in two identical twins affected by adenosine deaminase 2 deficiency.
Journal: Frontiers in immunology
Published: March 31, 2022
A Novel Assay in Whole Blood Demonstrates Restoration of Mitochondrial Activity in Phagocytes After Successful HSCT in Hyperinflamed X-Linked Chronic Granulomatous Disease.
Journal: Journal of clinical immunology
Published: February 06, 2022
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome.
Journal: The New England journal of medicine
Published: November 17, 2021
Wiskott-Aldrich syndrome: Oral findings and microbiota in children and review of the literature.
Journal: Clinical and experimental dental research
Published: June 16, 2021
Peripheral blood stem and progenitor cell collection in pediatric candidates for ex vivo gene therapy: a 10-year series.
Journal: Molecular therapy. Methods & clinical development
Published: April 08, 2021
Last Updated: 09/26/2026