Manuel V. Goncalves
Albert Einstein Allee 11
Ulm, BW 89081, Germany
Ulm, BW 89081, Germany
Last Updated: 09/26/2026
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Found 67 publications
Photoporation enables non-viral delivery of prime editing RNP complexes into human iPSC-derived cardiomyocytes for cardiac genome correction.
Journal: Biomedicine & pharmacotherapy = Biomedecine & pharmacotherapie
Published: February 18, 2026
CRISPR-Cas9-mediated knock-in of cytomegalovirus US2 provides an alternative strategy for generating hypoimmunogenic hiPSC lines.
Journal: Scientific reports
Published: January 16, 2026
LAH5-mediated delivery of prime editor ribonucleoprotein complexes for genome editing.
Journal: International journal of pharmaceutics
Published: October 27, 2025
Selector adeno-associated viral vectors facilitate on-target precise genome editing and purge off-target chromosomal insertions.
Journal: Trends in biotechnology
Published: June 23, 2025
Advanced delivery systems for gene editing: A comprehensive review from the GenE-HumDi COST Action Working Group.
Journal: Molecular therapy. Nucleic acids
Published: February 24, 2025
Comparative Analysis of Methods for Assessing On-Target Gene Editing Efficiencies.
Journal: Methods and protocols
Published: December 09, 2024
Conventional and Tropism-Modified High-Capacity Adenoviral Vectors Exhibit Similar Transduction Profiles in Human iPSC-Derived Retinal Organoids.
Journal: International journal of molecular sciences
Published: November 20, 2024
Integrating Prime Editing and Cellular Reprogramming as Novel Strategies for Genetic Cardiac Disease Modeling and Treatment.
Journal: Current cardiology reports
Published: August 12, 2024
Donor insertion into CX3CR1 allows epigenetic modulation of a constitutive promoter on hematopoietic stem cells and its activation upon myeloid differentiation.
Journal: Nucleic acids research
Published: August 12, 2024
On RNA-programmable gene modulation as a versatile set of principles targeting muscular dystrophies.
On RNA-programmable gene modulation as a versatile set of principles targeting muscular dystrophies.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: May 05, 2024
Last Updated: 09/26/2026