Last Updated: 09/26/2026
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Found 51 publications
Comparative analysis of microglia-targeted AAVs reveals capsid choice drives efficiency in vitro but has limited impact in vivo.
Journal: bioRxiv : the preprint server for biology
Published: August 20, 2026
Normative modeling for quantitative brain MRI phenotyping and biomarker discovery for pediatric leukodystrophies.
Journal: medRxiv : the preprint server for health sciences
Published: June 05, 2026
CNS engraftment after HCT: Making the niche more accessible.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: April 13, 2026
PTPN1-related autoinflammation is a common cause of Aicardi-Goutières Syndrome with reduced penetrance.
Journal: medRxiv : the preprint server for health sciences
Published: April 10, 2026
PTPN1 -related autoinflammation is a common cause of Aicardi-Goutières Syndrome with reduced penetrance.
Journal: medRxiv : the preprint server for health sciences
Published: April 10, 2026
Movement Disorders in Aicardi-Goutières Syndrome and Response to Immunomodulation.
Journal: Annals of clinical and translational neurology
Published: February 08, 2026
Microglia replacement by ER-Hoxb8 conditionally immortalized macrophages provides insight into Aicardi-Goutières syndrome neuropathology.
Journal: eLife
Published: January 27, 2026
Basic Microglial Functions and How They Go Awry in Neurodegenerative Disease.
Journal: Annual review of pathology
Published: January 26, 2026
Microglial MEF2C is a uniquely human bridge between neurodevelopment and neurodegeneration.
Journal: Nature immunology
Published: October 22, 2025
Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study.
Journal: Annals of the Child Neurology Society
Published: August 26, 2025
Targeting DNA-LNPs to Endothelial Cells Improves Expression Magnitude, Duration, and Specificity.
Journal: Advanced science (Weinheim, Baden-Wurttemberg, Germany)
Published: August 12, 2025
Targeting DNA-LNPs to Endothelial Cells Improves Expression Magnitude, Duration, and Specificity.
Journal: bioRxiv : the preprint server for biology
Published: July 17, 2025
Last Updated: 09/26/2026