Last Updated: 09/26/2026
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Found 41 publications
Calling for a strategic shift in drug development for childhood cancers.
Journal: The Lancet. Child & adolescent health
Published: June 13, 2026
Considerations for Clinical Trial Design in Relapsed and Refractory Osteosarcoma: An FDA Symposium.
Journal: Clinical cancer research : an official journal of the American Association for Cancer Research
Published: September 09, 2025
Paediatric Strategy Forum for medicinal product development of agents targeting GD2 ganglioside in children and adolescents with cancer.
Journal: European journal of cancer (Oxford, England : 1990)
Published: July 29, 2025
Rare cancers research: Current state of knowledge and emerging opportunities for prevention and interception.
Journal: Journal of the National Cancer Institute
Published: June 17, 2025
How to foster new treatment development in ultra-rare tumours? Joint EMA-EORTC multi-stakeholder workshops on ultra-rare sarcomas as a model for rare cancers.
Journal: Cancer treatment reviews
Published: June 13, 2025
Dosage Optimization of Pediatric Oncology Products: Our Patients Deserve Better.
Journal: Clinical cancer research : an official journal of the American Association for Cancer Research
Published: January 07, 2025
Paediatric strategy forum for medicinal product development in diffuse midline gliomas in children and adolescents ACCELERATE in collaboration with the European Medicines Agency with participation of the Food and Drug Administration.
Journal: European journal of cancer (Oxford, England : 1990)
Published: November 14, 2024
FDA Approval Summary: Tovorafenib for Relapsed or Refractory BRAF-Altered Pediatric Low-Grade Glioma.
Journal: Clinical cancer research : an official journal of the American Association for Cancer Research
Published: October 17, 2024
US Food and Drug Administration Approval Summary: Eflornithine for High-Risk Neuroblastoma After Prior Multiagent, Multimodality Therapy.
Journal: Journal of clinical oncology : official journal of the American Society of Clinical Oncology
Published: June 25, 2024
Review of Racial and Ethnic Representation of Participants Enrolled in Pediatric Clinical Trials of Oncology Drugs Conducted Through FDA Written Requests.
Journal: JAMA oncology
Published: January 04, 2024
Paediatric strategy forum for medicinal product development of PI3-K, mTOR, AKT and GSK3β inhibitors in children and adolescents with cancer.
Journal: European journal of cancer (Oxford, England : 1990)
Published: November 23, 2023
Considering Functional Outcomes as Efficacy Endpoints in Pediatric Low-Grade Glioma Clinical Trials: An FDA Educational Symposium.
Journal: Clinical cancer research : an official journal of the American Association for Cancer Research
Published: November 03, 2023
Last Updated: 09/26/2026