Last Updated: 09/26/2026
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Found 162 publications
Unlocking the curative potential of gene transfer and editing for hematopoietic disorders.
Journal: Experimental hematology
Published: May 18, 2026
Endothelial Cell Secretome Alterations Induced by Inflammatory Stress.
Journal: bioRxiv : the preprint server for biology
Published: February 06, 2026
The Longitudinal Effect of APOL1 Risk Alleles on Sickle Cell Anemia-Associated Kidney Function.
Journal: American journal of hematology
Published: December 29, 2025
A new advance in therapeutic induction of fetal hemoglobin on an uncertain road to durable access.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: December 02, 2025
Disrupting epigenetic insulation underlies CRISPR therapy for β-hemoglobinopathies.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: December 01, 2025
The H3K4 methyltransferase KMT2D is an essential cofactor for GATA1 at erythroid gene enhancers.
Journal: Nature communications
Published: October 13, 2025
RPS19 and RPL5 haploinsufficient models reveal divergent ribosomal subunit controls of fetal hematopoiesis.
Journal: Nature communications
Published: September 11, 2025
Generation of iPSC and isogenic gene-corrected lines from a patient with RPS7 (c.277_279delGTC)-mutated Diamond-Blackfan anemia syndrome.
Journal: Stem cell research
Published: August 28, 2025
Engraftment and persistence of HBB base-edited hematopoietic stem cells in nonhuman primates.
Journal: Science translational medicine
Published: August 13, 2025
Last Updated: 09/26/2026