Monica Volpin
Milan, 20132, Italy
Last Updated: 09/26/2026
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Found 11 publications
Tweaking lentiviral vector design balances efficacy and safety in liver-directed gene therapy for familial hypercholesterolemia.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: October 14, 2025
Ex vivo expansion of hematopoietic stem and progenitor cells from human mobilized peripheral blood for gene therapy applications.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: October 10, 2025
Spatiotemporal liver dynamics shape hepatocellular heterogeneity and impact in vivo gene engineering.
Journal: Journal of hepatology
Published: August 23, 2024
Enhancing the potency of in vivo lentiviral vector mediated gene therapy to hepatocytes.
Journal: Nature communications
Published: July 01, 2024
In vivo haemopoietic stem cell gene therapy enabled by postnatal trafficking.
Journal: Nature
Published: February 08, 2024
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID.
Journal: Nature communications
Published: October 13, 2023
Balanced SET levels favor the correct enhancer repertoire during cell fate acquisition.
Journal: Nature communications
Published: October 26, 2022
Longitudinal single-cell profiling of chemotherapy response in acute myeloid leukemia.
Journal: Nature communications
Published: December 16, 2021
Investigating the Barrier Activity of Novel, Human Enhancer-Blocking Chromatin Insulators for Hematopoietic Stem Cell Gene Therapy.
Journal: Human gene therapy
Published: September 03, 2021
Liver-directed lentiviral gene therapy in a dog model of hemophilia B.
Journal: Science translational medicine
Published: March 06, 2015
Uncovering and dissecting the genotoxicity of self-inactivating lentiviral vectors in vivo.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: November 06, 2013
Showing 1-11 of 11
Last Updated: 09/26/2026