Last Updated: 09/26/2026
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Found 5 publications
Early Intervention and Speed-to-Effect in Spinal Muscular Atrophy Type 1 Following Onasemnogene Abeparvovec Gene Replacement Therapy: Results of aPost-Hoc Analysis of Pooled Clinical Study Data.
Journal: Neurology and therapy
Published: May 14, 2025
Safety and tolerability of onasemnogene abeparvovec for patients with spinal muscular atrophy weighing ≤17 kg and ≤24 months old from OFELIA, a phase 4, open-label, multicenter, non-randomised, interventional study.
Journal: Lancet regional health. Americas
Published: March 12, 2025
Adeno-associated virus serotype 9 antibodies in neonates and young children: Seroprevalence and kinetics.
Journal: Molecular therapy. Methods & clinical development
Published: July 24, 2024
Omalizumab in Asthma with Fixed Airway Obstruction: Post Hoc Analysis of EXTRA.
Journal: The journal of allergy and clinical immunology. In practice
Published: January 04, 2021
Angioedema with severe acute abdominal pain: Think of hereditary angioedema.
Journal: Clinics and research in hepatology and gastroenterology
Published: September 11, 2020
Showing 1-5 of 5
Last Updated: 09/26/2026