Nora P. Watman

Ramos Mejia, B, Argentina

Last Updated: 09/26/2026

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Found 11 publications

Argentine program of home infusions with enzyme replacement therapy for lysosomal diseases: Results in safety, quality of life and adherence.

Argentine program of home infusions with enzyme replacement therapy for lysosomal diseases: Results in safety, quality of life and adherence.

Journal: Molecular genetics and metabolism

Published: December 09, 2024

Pregnancy outcome in women with Gaucher disease type 1 who had unplanned pregnancies during eliglustat clinical trials.

Pregnancy outcome in women with Gaucher disease type 1 who had unplanned pregnancies during eliglustat clinical trials.

Journal: JIMD reports

Published: May 14, 2020

Outcomes after 8 years of eliglustat therapy for Gaucher disease type 1: Final results from the Phase 2 trial.

Outcomes after 8 years of eliglustat therapy for Gaucher disease type 1: Final results from the Phase 2 trial.

Journal: American journal of hematology

Published: July 20, 2018

Assessment of liver and cardiac iron overload using MRI in patients with chronic anemias in Latin American countries: results from ASIMILA study.

Assessment of liver and cardiac iron overload using MRI in patients with chronic anemias in Latin American countries: results from ASIMILA study.

Journal: Hematology (Amsterdam, Netherlands)

Published: April 18, 2018

Influence of TNF and IL6 gene polymorphisms on the severity of cytopenias in Argentine patients with myelodysplastic syndromes.

Influence of TNF and IL6 gene polymorphisms on the severity of cytopenias in Argentine patients with myelodysplastic syndromes.

Journal: Annals of hematology

Published: March 22, 2017

Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.

Eliglustat maintains long-term clinical stability in patients with Gaucher disease type 1 stabilized on enzyme therapy.

Journal: Blood

Published: December 19, 2016

Evaluation of Bone Mineral Density in Patients with Type 1 Gaucher Disease in Argentina.

Evaluation of Bone Mineral Density in Patients with Type 1 Gaucher Disease in Argentina.

Journal: Journal of clinical densitometry : the official journal of the International Society for Clinical Densitometry

Published: June 01, 2016

Skeletal involvement in Gaucher disease: An observational multicenter study of prognostic factors in the Argentine Gaucher disease patients.

Skeletal involvement in Gaucher disease: An observational multicenter study of prognostic factors in the Argentine Gaucher disease patients.

Journal: American journal of hematology

Published: March 08, 2016

Myelodysplastic syndromes in South America: a multinational study of 1080 patients.

Myelodysplastic syndromes in South America: a multinational study of 1080 patients.

Journal: American journal of hematology

Published: June 15, 2015

Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat.

Skeletal improvement in patients with Gaucher disease type 1: a phase 2 trial of oral eliglustat.

Journal: Skeletal radiology

Published: March 27, 2014

Eliglustat, an investigational oral therapy for Gaucher disease type 1: Phase 2 trial results after 4 years of treatment.

Eliglustat, an investigational oral therapy for Gaucher disease type 1: Phase 2 trial results after 4 years of treatment.

Journal: Blood cells, molecules & diseases

Published: March 03, 2014

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Last Updated: 09/26/2026