Last Updated: 09/26/2026
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Found 15 publications
Excellent Long-Term Survival and Immune Recovery With Reduced-Intensity Conditioning HCT in Inborn Errors of Immunity.
Journal: Transplantation and cellular therapy
Published: February 03, 2026
Newborn screening reduces survival disparities in SCID after stem cell transplant: A PIDTC report.
Journal: Journal of human immunity
Published: October 27, 2025
Expanded Newborn Screening Using Genome Sequencing for Early Actionable Conditions.
Journal: JAMA
Published: October 24, 2024
Hematopoietic cell transplantation for inborn errors of immunity: an update on approaches, outcomes and innovations.
Journal: Current opinion in pediatrics
Published: September 25, 2024
Measuring the effect of newborn screening on survival after haematopoietic cell transplantation for severe combined immunodeficiency: a 36-year longitudinal study from the Primary Immune Deficiency Treatment Consortium.
Journal: Lancet (London, England)
Published: December 09, 2022
Clofarabine for Lymphodepletion Before CAR-T-Cell Infusion: A Brief Case Report.
Journal: Journal of pediatric hematology/oncology
Published: November 29, 2022
Nore1 inhibits age-associated myeloid lineage skewing and clonal hematopoiesis but facilitates termination of emergency (stress) granulopoiesis.
Journal: The Journal of biological chemistry
Published: October 20, 2022
The diagnosis of severe combined immunodeficiency: Implementation of the PIDTC 2022 Definitions.
Journal: The Journal of allergy and clinical immunology
Published: August 18, 2022
Ruxolitinib ameliorates progressive anemia and improves survival during episodes of emergency granulopoiesis in Fanconi C-/- mice.
Journal: Experimental hematology
Published: October 25, 2021
Compound heterozygous protein C variants undetectable by common laboratory testing causing purpura fulminans after the neonatal period.
Journal: American journal of hematology
Published: May 22, 2020
Sirolimus for treatment of refractory primary warm autoimmune hemolytic anemia in children.
Journal: Blood cells, molecules & diseases
Published: March 14, 2020
Last Updated: 09/26/2026