Ophelie Vacca
Versailles, France
Last Updated: 09/26/2026
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Found 20 publications
Beyond muscle: Delivering RNA therapeutics to the CNS in Duchenne muscular dystrophy.
Journal: Journal of neuromuscular diseases
Published: July 30, 2025
Ineffective behavioral rescue despite partial brain Dp427 restoration by AAV9-U7-mediated exon 51 skipping in mdx52 mice.
Journal: Molecular therapy. Nucleic acids
Published: June 17, 2025
Levels of Exon-Skipping Are Not Artificially Overestimated Because of the Increased Affinity of Tricyclo-DNA-Modified Antisense Oligonucleotides to the Target DMD Exon.
Journal: Nucleic acid therapeutics
Published: July 24, 2024
Networking to Optimize Dmd exon 53 Skipping in the Brain of mdx52 Mouse Model.
Journal: Biomedicines
Published: September 19, 2023
Partial restoration of brain dystrophin by tricyclo-DNA antisense oligonucleotides alleviates emotional deficits in mdx52 mice.
Journal: Molecular therapy. Nucleic acids
Published: October 20, 2022
Abnormal Expression of Synaptic and Extrasynaptic GABAA Receptor Subunits in the Dystrophin-Deficient mdx Mouse.
Journal: International journal of molecular sciences
Published: July 18, 2022
Rescue of Defective Electroretinographic Responses in Dp71-Null Mice With AAV-Mediated Reexpression of Dp71.
Journal: Investigative ophthalmology & visual science
Published: February 13, 2020
Evidence of the involvement of dystrophin Dp71 in corneal angiogenesis.
Journal: Molecular vision
Published: December 11, 2018
Expression and localization of dystrophins and β-dystroglycan in the hypothalamic supraoptic nuclei of rat from birth to adulthood.
Journal: Acta histochemica
Published: August 01, 2018
Last Updated: 09/26/2026