Patrice Verpillat
Darmstadt, HE, Germany
Last Updated: 09/26/2026
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Found 53 publications
Corrigendum to "Learnings from a registry-based cohort study for spinal muscular atrophy disease" [Neuromuscular Disorders, Volume 59, February 2026, 106332].
Journal: Neuromuscular disorders : NMD
Published: March 28, 2026
Advancing pharmacogenomics in medicines regulation and clinical practice: a call for collaborative action.
Journal: Nature reviews. Drug discovery
Published: November 22, 2025
Assessing Overall Survival Benefits in Advanced Cancers: The Role of External Comparator Cohort Studies with Real-World Data.
Journal: Clinical pharmacology and therapeutics
Published: November 08, 2025
Learnings from a registry-based cohort study for spinal muscular atrophy disease.
Journal: Neuromuscular disorders : NMD
Published: June 20, 2025
Optimizing Patient Registries for Regulatory Decision Making - Key Learnings From an HMA/EMA Multistakeholder Workshop.
Journal: Clinical pharmacology and therapeutics
Published: December 05, 2024
First-line treatment patterns and overall survival in patients diagnosed with metastatic Merkel cell carcinoma in England from 2013 to 2020: results of a nationwide observational cohort study.
Journal: The British journal of dermatology
Published: October 08, 2024
Validation of Mortality Data Sources Compared to the National Death Index in the Healthcare Integrated Research Database.
Journal: Pragmatic and observational research
Published: September 27, 2024
Collaborative Real-World Evidence Among Regulators: Lessons and Perspectives.
Journal: Clinical pharmacology and therapeutics
Published: June 12, 2024
Leveraging patient experience data to guide medicines development, regulation, access decisions and clinical care in the EU.
Journal: Frontiers in medicine
Published: March 28, 2024
Trends in the Completeness and Validity of Sources of Death Data Against the National Death Index From 2010 to 2018.
Journal: Pharmacoepidemiology and drug safety
Published: January 31, 2024
Factors associated with receipt of systemic anticancer treatment for locally advanced or metastatic urothelial carcinoma in England: a population-based study.
Journal: Urologic oncology
Published: January 19, 2024
Last Updated: 09/26/2026