Patrick Thompson

Kingston, ON K7L3N6, Canada

Last Updated: 09/26/2026

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Found 12 publications

Correction: Vyas et al. Efficacy of Adeno-Associated Virus Serotype 9-Mediated Gene Therapy for AB-Variant GM2 Gangliosidosis. Int. J. Mol. Sci. 2023, 24, 14611.

Correction: Vyas et al. Efficacy of Adeno-Associated Virus Serotype 9-Mediated Gene Therapy for AB-Variant GM2 Gangliosidosis. Int. J. Mol. Sci. 2023, 24, 14611.

Journal: International journal of molecular sciences

Published: January 17, 2026

Circular RNA Profiling Identifies circ5078 as a BMPR2-Derived Regulator of Endothelial Proliferation and Stress Responses.

Circular RNA Profiling Identifies circ5078 as a BMPR2-Derived Regulator of Endothelial Proliferation and Stress Responses.

Journal: Arteriosclerosis, thrombosis, and vascular biology

Published: August 07, 2025

Efficacy of Adeno-Associated Virus Serotype 9-Mediated Gene Therapy for AB-Variant GM2 Gangliosidosis.

Efficacy of Adeno-Associated Virus Serotype 9-Mediated Gene Therapy for AB-Variant GM2 Gangliosidosis.

Journal: International journal of molecular sciences

Published: April 29, 2023

Investigating Immune Responses to the scAAV9-HEXM Gene Therapy Treatment in Tay-Sachs Disease and Sandhoff Disease Mouse Models.

Investigating Immune Responses to the scAAV9-HEXM Gene Therapy Treatment in Tay-Sachs Disease and Sandhoff Disease Mouse Models.

Journal: International journal of molecular sciences

Published: May 17, 2021

Treatment of GM2 Gangliosidosis in Adult Sandhoff Mice Using an Intravenous Self-Complementary Hexosaminidase Vector.

Treatment of GM2 Gangliosidosis in Adult Sandhoff Mice Using an Intravenous Self-Complementary Hexosaminidase Vector.

Journal: Current gene therapy

Published: May 13, 2021

Efficacy of a Bicistronic Vector for Correction of Sandhoff Disease in a Mouse Model.

Efficacy of a Bicistronic Vector for Correction of Sandhoff Disease in a Mouse Model.

Journal: Molecular therapy. Methods & clinical development

Published: September 29, 2018

Battery of Behavioral Tests Assessing General Locomotion, Muscular Strength, and Coordination in Mice.

Battery of Behavioral Tests Assessing General Locomotion, Muscular Strength, and Coordination in Mice.

Journal: Journal of visualized experiments : JoVE

Published: February 15, 2018

Systemic Gene Transfer of a Hexosaminidase Variant Using an scAAV9.47 Vector Corrects GM2 Gangliosidosis in Sandhoff Mice.

Systemic Gene Transfer of a Hexosaminidase Variant Using an scAAV9.47 Vector Corrects GM2 Gangliosidosis in Sandhoff Mice.

Journal: Human gene therapy

Published: May 21, 2016

Novel Vector Design and Hexosaminidase Variant Enabling Self-Complementary Adeno-Associated Virus for the Treatment of Tay-Sachs Disease.

Novel Vector Design and Hexosaminidase Variant Enabling Self-Complementary Adeno-Associated Virus for the Treatment of Tay-Sachs Disease.

Journal: Human gene therapy

Published: May 21, 2016

Construction of a hybrid β-hexosaminidase subunit capable of forming stable homodimers that hydrolyze GM2 ganglioside in vivo.

Construction of a hybrid β-hexosaminidase subunit capable of forming stable homodimers that hydrolyze GM2 ganglioside in vivo.

Journal: Molecular therapy. Methods & clinical development

Published: December 16, 2015

Retrovirus-Mediated Expression of E2A-PBX1 Blocks Lymphoid Fate but Permits Retention of Myeloid Potential in Early Hematopoietic Progenitors.

Retrovirus-Mediated Expression of E2A-PBX1 Blocks Lymphoid Fate but Permits Retention of Myeloid Potential in Early Hematopoietic Progenitors.

Journal: PloS one

Published: July 24, 2014

Structural basis of CBP/p300 recruitment in leukemia induction by E2A-PBX1.

Structural basis of CBP/p300 recruitment in leukemia induction by E2A-PBX1.

Journal: Blood

Published: September 14, 2012

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Last Updated: 09/26/2026