Patrizia G. Cristofori

Milan, Italy

Last Updated: 09/26/2026

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Found 21 publications

A comprehensive review of humanized mice applications in regulatory submissions for cell and gene therapy products.

A comprehensive review of humanized mice applications in regulatory submissions for cell and gene therapy products.

Journal: Veterinary pathology

Published: January 26, 2026

Tweaking lentiviral vector design balances efficacy and safety in liver-directed gene therapy for familial hypercholesterolemia.

Tweaking lentiviral vector design balances efficacy and safety in liver-directed gene therapy for familial hypercholesterolemia.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: October 14, 2025

Development and characterization of a model of mucopolysaccharidosis type IVA for evaluating therapies targeting bone disease.

Development and characterization of a model of mucopolysaccharidosis type IVA for evaluating therapies targeting bone disease.

Journal: Disease models & mechanisms

Published: June 27, 2025

Tumor-associated macrophages enhance peripheral nerve tumor infiltration and spinal cord repair.

Tumor-associated macrophages enhance peripheral nerve tumor infiltration and spinal cord repair.

Journal: Immunity

Published: July 31, 2024

In vivo armed macrophages curb liver metastasis through tumor-reactive T-cell rejuvenation.

In vivo armed macrophages curb liver metastasis through tumor-reactive T-cell rejuvenation.

Journal: Nature communications

Published: July 19, 2024

Toxicologic Pathology Forum: Opinion on Performing Good Laboratory Practice Histopathology Evaluation for Nonclinical Toxicity Studies in a Remote Location.

Toxicologic Pathology Forum: Opinion on Performing Good Laboratory Practice Histopathology Evaluation for Nonclinical Toxicity Studies in a Remote Location.

Journal: Toxicologic pathology

Published: April 26, 2023

Conditioning Regimens in Long-Term Pre-Clinical Studies to Support Development of Ex Vivo Gene Therapy: Review of Nonproliferative and Proliferative Changes.

Conditioning Regimens in Long-Term Pre-Clinical Studies to Support Development of Ex Vivo Gene Therapy: Review of Nonproliferative and Proliferative Changes.

Journal: Human gene therapy

Published: September 05, 2020

Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy.

Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: April 10, 2020

Ex Vivo Gene Therapy: Graft-versus-host Disease (GVHD) in NSG™ (NOD.Cg-Prkdcscid Il2rgtm1Wjl/SzJ) Mice Transplanted with CD34+ Human Hematopoietic Stem Cells.

Ex Vivo Gene Therapy: Graft-versus-host Disease (GVHD) in NSG™ (NOD.Cg-Prkdcscid Il2rgtm1Wjl/SzJ) Mice Transplanted with CD34+ Human Hematopoietic Stem Cells.

Journal: Toxicologic pathology

Published: May 09, 2019

Phagocytosis-shielded lentiviral vectors improve liver gene therapy in nonhuman primates.

Phagocytosis-shielded lentiviral vectors improve liver gene therapy in nonhuman primates.

Journal: Science translational medicine

Published: October 15, 2018

Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia.

Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia.

Journal: Molecular therapy. Methods & clinical development

Published: June 18, 2018

A Diagnostic Approach for Rodent Progressive Cardiomyopathy and Like Lesions in Toxicology Studies up to 28 Days in the Sprague Dawley Rat (Part 2 of 2).

A Diagnostic Approach for Rodent Progressive Cardiomyopathy and Like Lesions in Toxicology Studies up to 28 Days in the Sprague Dawley Rat (Part 2 of 2).

Journal: Toxicologic pathology

Published: December 14, 2017

Showing 1-12 of 21

Last Updated: 09/26/2026