Patrizia Tornabene
Pozzuoli, 80078, Italy
Last Updated: 09/26/2026
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Found 11 publications
Uncovering mitochondrial defects in photoreceptors opens therapeutic opportunities for Stargardt disease.
Journal: Proceedings of the National Academy of Sciences of the United States of America
Published: April 15, 2026
Microphysiological systems to accelerate and de-risk AAV gene therapy development.
Journal: Advanced drug delivery reviews
Published: November 26, 2025
Exploring optimal protocols for generating and preserving glucose-responsive insulin-secreting progenitor cells derived from human pluripotent stem cells.
Journal: European journal of cell biology
Published: April 01, 2024
Liver gene therapy with intein-mediated F8 trans-splicing corrects mouse haemophilia A.
Journal: EMBO molecular medicine
Published: October 13, 2021
Inclusion of a degron reduces levelsof undesired inteins after AAV-mediated proteintrans-splicing in the retina.
Journal: Molecular therapy. Methods & clinical development
Published: August 13, 2021
Therapeutic homology-independent targeted integration in retina and liver.
Journal: Nature communications
Published: January 04, 2021
Large gene delivery to the retina with AAV vectors: are we there yet?
Journal: Gene therapy
Published: March 30, 2020
Can Adeno-Associated Viral Vectors Deliver Effectively Large Genes?
Journal: Human gene therapy
Published: January 10, 2020
Intein-mediated protein trans-splicing expands adeno-associated virus transfer capacity in the retina.
Journal: Science translational medicine
Published: September 17, 2018
High-Throughput Screening Identifies Kinase Inhibitors That Increase Dual Adeno-Associated Viral Vector Transduction In Vitro and in Mouse Retina.
Journal: Human gene therapy
Published: April 12, 2018
Triple Vectors Expand AAV Transfer Capacity in the Retina.
Journal: Molecular therapy : the journal of the American Society of Gene Therapy
Published: May 07, 2017
Showing 1-11 of 11
Last Updated: 09/26/2026