Philippe Veron

1bis, Rue De L'Internationale
Evry, 91000, France

Last Updated: 09/26/2026

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Found 23 publications

Death following high-dose AAV9 gene therapy in a patient with advanced SMA-PME.

Death following high-dose AAV9 gene therapy in a patient with advanced SMA-PME.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: November 21, 2025

Identification of alterations of immunometabolism associated with Pompe disease.

Identification of alterations of immunometabolism associated with Pompe disease.

Journal: Cellular and molecular life sciences : CMLS

Published: August 20, 2025

Transgene-induced cardiotoxicity in high-dose AAV gene transfer.

Transgene-induced cardiotoxicity in high-dose AAV gene transfer.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: March 26, 2025

Repeated dosing of AAV-mediated liver gene therapy in juvenile rat and mouse models of Crigler-Najjar syndrome type I.

Repeated dosing of AAV-mediated liver gene therapy in juvenile rat and mouse models of Crigler-Najjar syndrome type I.

Journal: Molecular therapy. Methods & clinical development

Published: April 26, 2024

An engineered AAV targeting integrin alpha V beta 6 presents improved myotropism across species.

An engineered AAV targeting integrin alpha V beta 6 presents improved myotropism across species.

Journal: Nature communications

Published: October 25, 2023

Gene Therapy in Patients with the Crigler-Najjar Syndrome.

Gene Therapy in Patients with the Crigler-Najjar Syndrome.

Journal: The New England journal of medicine

Published: August 16, 2023

Analysis of Adeno-Associated Virus Serotype 8 (AAV8)-antibody complexes using epitope mapping by molecular imprinting leads to the identification of Fab peptides that potentially evade AAV8 neutralisation.

Analysis of Adeno-Associated Virus Serotype 8 (AAV8)-antibody complexes using epitope mapping by molecular imprinting leads to the identification of Fab peptides that potentially evade AAV8 neutralisation.

Journal: Nanomedicine : nanotechnology, biology, and medicine

Published: February 01, 2023

H-BIM and Artificial Intelligence: Classification of Architectural Heritage for Semi-Automatic Scan-to-BIM Reconstruction.

H-BIM and Artificial Intelligence: Classification of Architectural Heritage for Semi-Automatic Scan-to-BIM Reconstruction.

Journal: Sensors (Basel, Switzerland)

Published: January 25, 2023

Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B.

Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B.

Journal: Molecular therapy. Methods & clinical development

Published: November 09, 2022

Smartphone LiDAR Data: A Case Study for Numerisation of Indoor Buildings in Railway Stations.

Smartphone LiDAR Data: A Case Study for Numerisation of Indoor Buildings in Railway Stations.

Journal: Sensors (Basel, Switzerland)

Published: September 23, 2022

Liver-Directed Adeno-Associated Virus-Mediated Gene Therapy for Mucopolysaccharidosis Type VI.

Liver-Directed Adeno-Associated Virus-Mediated Gene Therapy for Mucopolysaccharidosis Type VI.

Journal: NEJM evidence

Published: July 01, 2022

Early Phase Clinical Immunogenicity of Valoctocogene Roxaparvovec, an AAV5-Mediated Gene Therapy for Hemophilia A.

Early Phase Clinical Immunogenicity of Valoctocogene Roxaparvovec, an AAV5-Mediated Gene Therapy for Hemophilia A.

Journal: Molecular therapy : the journal of the American Society of Gene Therapy

Published: July 13, 2020

Showing 1-12 of 23

Last Updated: 09/26/2026