Rajvinder Karda
86-96 Chenies Mews
London, ENG, United Kingdom
London, ENG, United Kingdom
Last Updated: 09/26/2026
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Found 28 publications
Next generation AAV-F capsid gene therapy rescues disease pathology in a model of pyruvate dehydrogenase complex deficiency.
Journal: Molecular therapy. Advances
Published: August 13, 2025
Safety and efficacy analysis of in vivo lentiviral gene therapy in pre-clinical ARC syndrome models.
Safety and efficacy analysis of in vivo lentiviral gene therapy in pre-clinical ARC syndrome models.
Journal: Nature communications
Published: May 15, 2025
AAV9-mediated targeting of natural antisense transcript as a novel treatment for Dravet syndrome.
Journal: Molecular therapy. Nucleic acids
Published: May 14, 2025
Creation of de novo cryptic splicing for ALS and FTD precision medicine.
Journal: Science (New York, N.Y.)
Published: October 03, 2024
Gene therapy prevents hepatic mitochondrial dysfunction in murine deoxyguanosine kinase deficiency.
Journal: Molecular therapy. Methods & clinical development
Published: June 02, 2024
Ascending Vaginal Infection in Mice Induces Preterm Birth and Neonatal Morbidity.
Journal: The American journal of pathology
Published: May 20, 2024
Creation of de novo cryptic splicing for ALS/FTD precision medicine.
Journal: bioRxiv : the preprint server for biology
Published: November 28, 2023
Systemic gene therapy rescues retinal dysfunction and hearing loss in a model of Norrie disease.
Journal: EMBO molecular medicine
Published: January 05, 2023
Genetic therapeutic advancements for Dravet Syndrome.
Journal: Epilepsy & behavior : E&B
Published: March 11, 2022
Rapid and inexpensive purification of adenovirus vectors using an optimised aqueous two-phase technology.
Journal: Journal of virological methods
Published: October 27, 2020
Re-structuring lentiviral vectors to express genomic RNA via cap-dependent translation.
Journal: Molecular therapy. Methods & clinical development
Published: March 06, 2020
Last Updated: 09/26/2026