Last Updated: 09/26/2026
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Found 23 publications
Red lines and green lights: Gene therapy for inherited erythroid disorders beyond the haemoglobinopathies.
Journal: British journal of haematology
Published: March 27, 2026
Systematic functional dissection of germline noncoding risk variants impacting clonal hematopoiesis.
Systematic functional dissection of germline noncoding risk variants impacting clonal hematopoiesis.
Journal: bioRxiv : the preprint server for biology
Published: February 06, 2026
Germline noncoding risk variants influence clonal hematopoiesis through altered hematopoietic enhancer activity.
Journal: Blood cancer discovery
Published: February 05, 2026
CEBPA repression by MECOM blocks differentiation to drive aggressive leukemias.
Journal: Blood
Published: March 03, 2025
CEBPA repression by MECOM blocks differentiation to drive aggressive leukemias.
Journal: bioRxiv : the preprint server for biology
Published: January 13, 2025
Regulated GATA1 expression as a universal gene therapy for Diamond-Blackfan anemia.
Journal: Cell stem cell
Published: March 28, 2024
Gene therapy for congenital marrow failure syndromes - no longer grasping at straws?
Journal: Haematologica
Published: June 01, 2023
MECOM Deficiency: from Bone Marrow Failure to Impaired B-Cell Development.
Journal: Journal of clinical immunology
Published: May 19, 2023
A genetic disorder reveals a hematopoietic stem cell regulatory network co-opted in leukemia.
Journal: Nature immunology
Published: February 22, 2022
Last Updated: 09/26/2026