Last Updated: 09/26/2026
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Found 2 publications
Pharmacokinetics and pharmacodynamics of PTC518, an oral huntingtin lowering splicing modifier: A first-in-human study.
Journal: British journal of clinical pharmacology
Published: January 30, 2024
Molecular diagnosis of somatic overgrowth conditions: A single-center experience.
Journal: Molecular genetics & genomic medicine
Published: July 25, 2018
Showing 1-2 of 2
Last Updated: 09/26/2026