Rongrong Zhang
Askim, O, Sweden
Last Updated: 09/26/2026
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Found 13 publications
Development of a face-validated conceptual model structure for economic evaluation in phenylketonuria, through expert elicitation.
Journal: Orphanet journal of rare diseases
Published: December 15, 2025
Eladocagene Exuparvovec for the Treatment of Aromatic L-Amino Acid Decarboxylase Deficiency (AADCd): An Economic Evaluation from a US Perspective.
Journal: PharmacoEconomics
Published: April 17, 2025
Intelligence quotient scores among early-treated phenylketonuria patients: results from a systematic literature review.
Journal: Orphanet journal of rare diseases
Published: January 14, 2025
Estimating health state utilities for aromatic L-amino acid decarboxylase deficiency (AADCd) in the United States.
Journal: Health and quality of life outcomes
Published: August 01, 2024
Clinically meaningful improvements after gene therapy for aromatic L-amino acid decarboxylase deficiency (AADCd) in the Peabody Developmental Motor Scale, Second Edition (PDMS-2) and correlation with Bayley-III scores and motor milestones.
Journal: Orphanet journal of rare diseases
Published: July 22, 2024
Predictors of cardiac disease in duchenne muscular dystrophy: a systematic review and evidence grading.
Journal: Orphanet journal of rare diseases
Published: November 15, 2023
Long-Term Outcomes of Eladocagene Exuparvovec Compared with Standard of Care in Aromatic L-Amino Acid Decarboxylase (AADC) Deficiency: A Modelling Study.
Journal: Advances in therapy
Published: July 29, 2023
A systematic review of disease prevalence, health-related quality of life, and economic outcomes associated with Friedreich's Ataxia.
Journal: Current medical research and opinion
Published: August 19, 2022
Assessment of face validity of a disease model of nonsense mutation Duchenne muscular dystrophy: a multi-national Delphi panel study.
Journal: Journal of medical economics
Published: June 01, 2022
Burden and severity of disease of aromatic L-amino acid decarboxylase deficiency: a systematic literature review.
Journal: Current medical research and opinion
Published: April 29, 2022
Adverse events in second- and third-line treatments for acute and chronic graft-versus-host disease: systematic review.
Journal: Therapeutic advances in hematology
Published: August 02, 2020
Systematic literature review of use of blood glucose monitoring in phase III clinical studies of insulin analogs.
Journal: BMC endocrine disorders
Published: November 15, 2015
Last Updated: 09/26/2026