Last Updated: 09/26/2026
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Found 19 publications
Gene Therapy for Sickle Cell Disease: Practice Recommendations from the American Society for Transplantation and Cellular Therapy and the International Society for Cell & Gene Therapy.
Journal: Transplantation and cellular therapy
Published: March 16, 2026
Gene Therapies for Transfusion-Dependent b-Thalassemia.
Journal: Indian pediatrics
Published: March 27, 2021
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia.
Journal: The New England journal of medicine
Published: December 07, 2020
Gene therapies for transfusion dependent β-thalassemia: Current status and critical criteria for success.
Journal: American journal of hematology
Published: February 10, 2020
A Phase 2 Trial of KIR-Mismatched Unrelated Donor Transplantation Using in Vivo T Cell Depletion with Antithymocyte Globulin in Acute Myelogenous Leukemia: Children's Oncology Group AAML05P1 Study.
Journal: Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Published: July 23, 2019
Chemistry, manufacturing and controls for gene modified hematopoietic stem cells.
Journal: Cytotherapy
Published: October 01, 2018
Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia.
Journal: The New England journal of medicine
Published: April 19, 2018
Unrelated Donor Transplantation in Children with Thalassemia using Reduced-Intensity Conditioning: The URTH Trial.
Journal: Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Published: December 03, 2017
Veno-occlusive disease after high-dose busulfan-melphalan in neuroblastoma.
Journal: Bone marrow transplantation
Published: August 28, 2017
Outcomes of Unrelated Donor Stem Cell Transplantion with Post-Transplant Cyclophosphamide for Graft-versus-Host Disease Prophylaxis in Patients with Severe Sickle Cell Disease.
Journal: Biology of blood and marrow transplantation : journal of the American Society for Blood and Marrow Transplantation
Published: August 02, 2017
Last Updated: 09/26/2026