Last Updated: 09/26/2026
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Found 7 publications
NGLY1 deficiency: a prospective natural history study.
Journal: Human molecular genetics
Published: May 05, 2023
NGLY1 deficiency: estimated incidence, clinical features, and genotypic spectrum from the NGLY1 Registry.
Journal: Orphanet journal of rare diseases
Published: June 16, 2022
Fostamatinib for the treatment of warm antibody autoimmune hemolytic anemia: Phase 2, multicenter, open-label study.
Journal: American journal of hematology
Published: October 06, 2021
Fostamatinib is an effective second-line therapy in patients with immune thrombocytopenia.
Journal: British journal of haematology
Published: April 04, 2020
Long-term fostamatinib treatment of adults with immune thrombocytopenia during the phase 3 clinical trial program.
Journal: American journal of hematology
Published: November 25, 2018
The measurement of physical functioning among patients with Tenosynovial Giant Cell Tumor (TGCT) using the Patient-Reported Outcomes Measurement Information System (PROMIS).
Journal: Journal of patient-reported outcomes
Published: May 10, 2018
Patient-reported Symptoms of Tenosynovial Giant Cell Tumors.
Journal: Clinical therapeutics
Published: December 29, 2015
Showing 1-7 of 7
Last Updated: 09/26/2026