Sandra Le Quellec
Faculté De Médecine Lyon Est
Lyon, France
Lyon, France
Last Updated: 09/26/2026
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Found 38 publications
Reply to a letter from Miesbach and Srivastava: response to hemophilia B gene therapy based on adeno-associated virus serotype 5 antibody status.
Journal: Research and practice in thrombosis and haemostasis
Published: March 06, 2026
Final Analysis of a Study of Etranacogene Dezaparvovec for Hemophilia B.
Journal: The New England journal of medicine
Published: December 08, 2025
Etranacogene dezaparvovec in people with hemophilia B with preexisting adeno-associated virus 5 neutralizing antibodies: 4-year subgroup results from the HOPE-B trial.
Journal: Research and practice in thrombosis and haemostasis
Published: November 03, 2025
Etranacogene dezaparvovec in people with hemophilia B and without adeno-associated virus serotype 5 neutralizing antibodies: a 4-year subgroup analysis of the Health Outcomes with Padua Gene; Evaluation in Hemophilia B (HOPE-B) trial.
Journal: Research and practice in thrombosis and haemostasis
Published: August 31, 2025
Natural history of preexisting AAV5 antibodies in adults with hemophilia B during the lead-in of the etranacogene dezaparvovec phase 3 study.
Journal: Molecular therapy. Methods & clinical development
Published: February 10, 2025
Invasive procedures and surgery following etranacogene dezaparvovec gene therapy in people with hemophilia B.
Journal: Journal of thrombosis and haemostasis : JTH
Published: April 04, 2024
A 360-degree perspective on adeno-associated virus (AAV)-based gene therapy for haemophilia: Insights from the physician, the nurse and the patient.
Journal: Orphanet journal of rare diseases
Published: March 05, 2024
Etranacogene dezaparvovec gene therapy for haemophilia B (HOPE-B): 24-month post-hoc efficacy and safety data from a single-arm, multicentre, phase 3 trial.
Journal: The Lancet. Haematology
Published: October 04, 2023
Gene therapy for haemophilia A and B, from basic principles to clinical implementation: An illustrated review.
Journal: Haemophilia : the official journal of the World Federation of Hemophilia
Published: July 17, 2023
In vivo intranasal delivery of coagulation factor IX: a proof-of-concept study.
Journal: Journal of thrombosis and haemostasis : JTH
Published: May 30, 2023
Stable and durable factor IX levels in patients with hemophilia B over 3 years after etranacogene dezaparvovec gene therapy.
Journal: Blood advances
Published: September 12, 2022
Last Updated: 09/26/2026