Last Updated: 09/26/2026
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Found 7 publications
The Target ALS Global Natural History Study: Cross-platform proteomics to accelerate biofluid biomarker and drug target discovery in amyotrophic lateral sclerosis.
Journal: medRxiv : the preprint server for health sciences
Published: July 03, 2026
A prospective, multi-center, observational study of the safety, tolerability and effectiveness of Nusinersen in adult patients with spinal muscular atrophy.
Journal: Neuromuscular disorders : NMD
Published: June 18, 2025
A prospective, multi-center, observational study of the safety, tolerability and effectiveness of Nusinersen in adult patients with spinal muscular atrophy.
Journal: Neuromuscular disorders : NMD
Published: June 18, 2025
CNM-Au8 in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial.
Journal: JAMA
Published: March 11, 2025
Pridopidine in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial.
Journal: JAMA
Published: March 11, 2025
Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis: A Randomized Clinical Trial.
Journal: JAMA network open
Published: February 17, 2025
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Last Updated: 09/26/2026