Last Updated: 09/26/2026
Save publications for later
Sign Up
Not sure about your diagnosis?
Check Your Symptoms
Found 36 publications
Adherence, treatment utilization, clinical and economic outcomes of patients with sickle cell disease with recurrent vaso-occlusive crises treated with recently approved chronic therapies in the US.
Journal: Journal of comparative effectiveness research
Published: November 24, 2025
Prospective case-control cohort analysis of two-day/two-stage pelvic exenteration surgery: Safety, feasibility, acceptability and medium-term outcomes.
Journal: Colorectal disease : the official journal of the Association of Coloproctology of Great Britain and Ireland
Published: September 29, 2025
Clinical characteristics and real-world outcomes in patients with mucopolysaccharidosis II over 18 years: final report of the Hunter Outcome Survey.
Journal: Molecular genetics and metabolism
Published: July 04, 2025
Long-term effectiveness and safety outcomes in adults with Fabry disease treated with agalsidase alfa: 20 years of data from the Fabry Outcome Survey.
Journal: European journal of clinical investigation
Published: June 26, 2025
Reply to Zhang et al.
Journal: Pediatric allergy and immunology : official publication of the European Society of Pediatric Allergy and Immunology
Published: June 02, 2025
Strategy to Enhance the Collapse Capacity of Composite Cylindrical Tubes: Experiments and Simulations.
Journal: Materials (Basel, Switzerland)
Published: February 18, 2025
Clinical and Economic Burden of Managing Patients with Sickle Cell Disease Receiving Frequent Red Blood Cell Transfusions in the United States.
Journal: ClinicoEconomics and outcomes research : CEOR
Published: December 17, 2024
Hereditary angioedema diagnosis: Reflecting on the past, envisioning the future.
Journal: The World Allergy Organization journal
Published: December 06, 2024
Effective long-term prophylaxis with lanadelumab in adolescents with hereditary angioedema: EMPOWER/ENABLE.
Journal: Pediatric allergy and immunology : official publication of the European Society of Pediatric Allergy and Immunology
Published: November 14, 2024
An international observational study on transition of care from paediatric to adult services for patients with mucopolysaccharidosis II.
Journal: BMC health services research
Published: November 01, 2024
Exposure to Operative Anesthesia in Childhood and Subsequent Neurobehavioral Diagnoses: A Natural Experiment Using Appendectomy.
Journal: Anesthesiology
Published: May 16, 2024
Last Updated: 09/26/2026